Prince Frederik of Luxembourg Dies at 22 of Rare Disease He Led Foundation to Research
Prince Frederik of Luxembourg dies at 22 from rare mitochondrial disease
Luxembourg’s Prince Frederik dead at 22 from rare genetic disease: ‘He is my superhero’
Florida Politics8h
Adam Anderson’s ‘Sunshine Genetics Act’ advances, offering promise for rare disease research and treatment
Ensuring every newborn has access to life-saving screening and treatment is both a moral and economic imperative.'
Rare Disease Day 2025: Know Date, History, Significance And More
Rare Disease Day is observed annually on the last day of February to raise awareness for the 300 million people worldwide living with a rare disease, their families, and carers. The day aims to improve the lives of those living with rare diseases by promoting equity in social opportunity,
FSU's Rare Disease Day spotlights promising research for families
Rare Disease Day provided a forum for university and state leaders to lay out the future plans and share the work already underway.
Jacobs School of Medicine and Biomedical Sciences - University at Buffalo4d
Rare Disease Day Event Focuses on Raising Awareness
UB hosted a Rare Disease Day program at the Jacobs School of Medicine and Biomedical Sciences to raise awareness of rare diseases.
Fierce Pharma11d
Arrowhead, Zevra fire up campaigns for Rare Disease Day 2025
Zevra used the awareness day to roll out the “Learn NPC, Read Between the Signs” disease awareness campaign. The biotech won FDA approval for a Niemann-Pick disease type C (NPC) treatment, Miplyffa, last year and recently agreed to sell a priority review voucher for $150 million to fund the launch and other work.