The potential target, the FLT1 gene, contributes to the production of a protein, fetal hemoglobin, whose presence is already ...

Scientists have discovered more than a dozen genes that regulate the production of fetal hemoglobin in people of African ...

Sebastien Beauzile became the first person in NY to be made symptom-free after undergoing a new type of gene therapy.

Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New York Post.

Sickle Cell Disease is a genetic blood disorder that affects hemoglobin, causing red blood cells to become rigid and sickle-shaped. These abnormal cells can block blood flow and lead to various ...

Scientists say they have identified a potential new gene target that could be edited to treat sickle cell disease, an ...

Scientists have found a potential new gene variant target to treat sickle cell disease, an inherited blood disorder that ...

“Now he’s producing normal adult hemoglobin in his parent cells. You see it in his blood as well,” Dr. Aygun said. “That’s why he’s not having any symptoms related to his sickle cell ...

Feb. 25, 2025 — A bone marrow transplant process is safe and curative for adults with sickle cell disease, according to results of a trial completed at about 20 cancer ... Brains of People With ...

A toolkit on hydroxyurea was designed to help parents of young children with sickle cell disease feel more confident about choosing treatment.

Sickle cell anemia is the most common inherited blood disorder and affects roughly 100,000 people in the United States at a given time. It's caused by a mutation of the hemoglobin gene ...

According to the U.S. Center for Disease Control and Prevention, "sickle cell disease (SCD) is a group of inherited blood disorders. Red blood cells contain hemoglobin, a protein that carries oxygen.