The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.
13don MSN
US astronauts Butch Wilmore and Suni Williams are finally coming home — here are some of the health issues they may ...
2d
Independent.ie on MSN‘Every day counts’- call to add screening for rare muscle-wasting condition to newborns’ ‘heel prick’ testA majority of people have supported the urgent implementation of early screening for a genetic disease that causes severe muscle degeneration.The last government promised to add the test for spinal ...
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
“We were referred to a paediatrician who put him on reflux medication. However, things were getting worse,” Ellie said. “He ...
2d
LancsLive on MSN'We waited months for answers over our baby's condition - now he'll never be able to walk'Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...
Video: Spinal Muscular Atrophy: When is Surgical Intervention Appropriate? —How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit ...
Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...
A rare genetic condition, Spinal Muscular Atrophy (SMA) affects one in 7,000 people in India. It mostly affects children and ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results