New gene therapy cures 1st New Yorker of sickle cell anemia

Sickle cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy.
Long Island patient gets breakthrough sickle cell treatment called a ‘cure’: ‘I’m not in pain anymore’
A young man from Laurelton is the first New Yorker with sickle cell disease to receive Lyfgenia, a life-changing gene therapy treatment that has wiped away the debilitating illness, The Post first
Long Island man is first in New York history to be cured of sickle cell anemia
A patient on Long Island is the first in New York to be cured of sickle cell anemia, doctors say. They credit state-of-the-art genetic treatment. Medical history made at Cohen Children's Medical Center For 21 years,
Gene therapy cures man from sickle cell
A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life. He was Sebastien Beauzile was born with sickle cell anemia and struggled to live a pain free life. However,
'I'm Unstoppable': New gene therapy cures first New Yorker of sickle cell anemia
Thanks to his medical team, Sebastien is grateful for becoming the first person in New York to receive a new genetic treatment, Lyfgenia, to cure his sickle cell disease.
LVB1d
Helping Employers Prepare for Gene and Cellular Therapies
Cellular therapy, according to the Dana-Farber Cancer Institute, is designed to improve the immune system’s ability to fight ...
BioPharma Dive4d
3 ways to accelerate development and de-risk cell and gene therapy manufacturing
Development strategies designed to reduce the unknowns so that cell and gene therapy innovators can develop robust processes ...
EurekAlert!2d
IL2RG gene therapy for X-SCID
X-linked severe combined immunodeficiency disease (X-SCID) is a rare genetic disorder characterized by profound defects in ...
Pharmaceutical Commerce16h
Breaking Down Regulatory Challenges in Cell Therapy Production
In the third part of his video interview with Pharma Commerce Editor Nicholas Saraceno, Jason C. Foster, CEO of Ori Biotech, ...
Live Science on MSN1d
POLG diseases: Rare genetic conditions that starve cells of energy and afflicted the late Prince of Luxembourg
POLG-related diseases disrupt the function of the mitochondria, or "powerhouses" of the cell — starving them of energy.
Using machine learning tools to detect gene mutations from leukemia cell images
Gene mutations in acute myeloid leukemia (AML) cells can guide treatment options, and machine learning can rapidly guess the existence of gene mutations based on images of leukemia cells.
Pharmaceutical Commerce3d
Unlocking the Potential of Cell and Gene Therapies
In the first part of his video interview with Pharma Commerce Editor Nicholas Saraceno, Jason C. Foster, CEO of Ori Biotech, offers his perspective on the state of CGTs, along with their potential for ...
Business Wire1d
ENCell Signs MOU with Cell Resources Corporation to Pave Way for Market Entry to Japan
ENCell inks an MOU with CRC to enhance collaboration in the field of cell and gene therapy (CGT), thus expanding its market ...
Gene related to human kidney disease linked to touch in sea anemones
Biological sciences researchers from the U of A have led the publication of a paper that expands our understanding of sensory ...
CRISPR cut a gene from head and neck cancers -through direct injection
Researchers from Tel Aviv University utilized CRISPR to cut a single gene from cancer cells of head and neck tumors – and ...